| Issue |
Med Sci (Paris)
Volume 37, Number 10, Octobre 2021
|
|
|---|---|---|
| Page(s) | 933 - 935 | |
| Section | Forum | |
| DOI | https://doi.org/10.1051/medsci/2021140 | |
| Published online | 14 October 2021 | |
Édition de gènes in vivo et thérapie génique
Chroniques génomiques
In vivo gene editing for gene therapy
ADÉS (Anthropologie bio-culturelle, droit, éthique et santé) UMR CNRS 7268, Aix Marseille université, Établissement français du sang.CoReBio PACA, case 901, Parc scientifique de Luminy, 13288 Marseille Cedex 09, France
Abstract
In vivo gene editing has been achieved in a phase I clinical trial and results in a strong reduction of the level of a pathogenic protein. While preliminary, these results open the way for many applications in gene therapy.
© 2021 médecine/sciences – Inserm
Article publié sous les conditions définies par la licence Creative Commons Attribution License CC-BY (https://creativecommons.org/licenses/by/4.0), qui autorise sans restrictions l'utilisation, la diffusion, et la reproduction sur quelque support que ce soit, sous réserve de citation correcte de la publication originale.
Current usage metrics show cumulative count of Article Views (full-text article views including HTML views, PDF and ePub downloads, according to the available data) and Abstracts Views on Vision4Press platform.
Data correspond to usage on the plateform after 2015. The current usage metrics is available 48-96 hours after online publication and is updated daily on week days.
Initial download of the metrics may take a while.